This #InternationalPompeDay#, watch Benedikt Schoser, Priya Sunil Kishnani, and @MozaffarTahseen discuss unmet needs in late‑onset Pompe disease, now available on the NEW Medthority Rare Disease Nexus for expert insights and CME
To mark #InternationalPompeDay#, new survey data highlight persistent challenges in late‑onset Pompe disease care, from delayed diagnostic journeys to unmet supportive needs. Read the latest insights